IONIS PHARMACEUTICALS INC
Phase 3 Confirmed
zilganersen
Alexander disease
Resolved
77days ago
Phase 3 readout · Apr 21, 2026
What's at stake Phase 3 trial results for zilganersen in Alexander disease are due Apr 21, 2026. A clean hit validates the program; a miss can gap the stock down hard.
“Additionally, results from the GMFM-88 in children 2-4 years of age support that zilganersen may improve gross motor function at Week 61 compared to control (least square mean difference 22.9 points, nominal 1 p=0.034).”

Provenance

6 sources on file.

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